Gene therapy helps dogs with muscle dystrophy, humans next?
Researchers have used gene editing to reverse symptoms in dogs of Duchenne muscular dystrophy (DMD)—a muscle-wasting and life-shortening disease that affects one in 5,000 baby boys.
Researchers have used gene editing to reverse symptoms in dogs of Duchenne muscular dystrophy (DMD)—a muscle-wasting and life-shortening disease that affects one in 5,000 baby boys.
Biotechnology
Jul 25, 2017
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386
(PhysOrg.com) -- Chemists at the University at Buffalo have used rational drug design to synthesize small, cell-permeable molecules that are effective in vitro against two common types of myotonic muscular dystrophy, a result ...
Biochemistry
Aug 7, 2009
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Many scientists use animals to model human diseases. Mice can be obese or display symptoms of Parkinson's disease. Rats get Alzheimer's and diabetes.
Cell & Microbiology
Jun 27, 2013
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Researchers from the University of Minnesota's Lillehei Heart Institute have effectively treated muscular dystrophy in mice using human stem cells derived from a new process that for the first time makes the ...
Cell & Microbiology
May 4, 2012
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A research study has shed new light on how congenital muscular dystrophies such as Walker-Warburg syndrome progress, bringing hope for better understanding, early diagnosis and treatments of these fatal disorders.
Molecular & Computational biology
Mar 10, 2023
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233
(Phys.org)—Imagine not being able to touch a touch-screen device. Tablets and smartphones—with all their educational, entertaining and social benefits—would be useless.
Hi Tech & Innovation
Dec 11, 2012
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There's a revolution happening in biology, and its name is CRISPR.
Biotechnology
May 18, 2017
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38
When you lift weights, carry heavy boxes, or engage in physical activity, the cells in your body stretch and deform to accommodate your movements. But how do your cells recover, or return to their original state, once you ...
Biotechnology
Jun 20, 2017
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Using high-resolution electron microscopy, Columbia University Medical Center (CUMC) researchers have uncovered new details of the structure and function of an intracellular channel that controls the contraction of skeletal ...
Biochemistry
Sep 22, 2016
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University at Buffalo biophysicists have found a protein in tarantula venom that shows promise as a potential therapy for muscular dystrophy (MD). They have formed a start-up biotech company in Buffalo -- Rose Pharmaceuticals ...
Biotechnology
Dec 29, 2009
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