Gene therapy helps dogs with muscle dystrophy, humans next?
Researchers have used gene editing to reverse symptoms in dogs of Duchenne muscular dystrophy (DMD)—a muscle-wasting and life-shortening disease that affects one in 5,000 baby boys.
Researchers have used gene editing to reverse symptoms in dogs of Duchenne muscular dystrophy (DMD)—a muscle-wasting and life-shortening disease that affects one in 5,000 baby boys.
Biotechnology
Jul 25, 2017
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386
When you lift weights, carry heavy boxes, or engage in physical activity, the cells in your body stretch and deform to accommodate your movements. But how do your cells recover, or return to their original state, once you ...
Biotechnology
Jun 20, 2017
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22
Using 3-D electron microscopy, structural biologists from the University of Zurich succeeded in elucidating the architecture of the lamina of the cell nucleus at molecular resolution for the first time. This scaffold stabilizes ...
Biochemistry
Mar 1, 2017
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713
Using high-resolution electron microscopy, Columbia University Medical Center (CUMC) researchers have uncovered new details of the structure and function of an intracellular channel that controls the contraction of skeletal ...
Biochemistry
Sep 22, 2016
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13
Researchers in Singapore have developed a new protein that can alter DNA in living cells with much higher precision than current methods.
Biochemistry
Sep 13, 2016
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203
Efforts to treat myotonic dystrophy type 1, the most common form of muscular dystrophy, are in their infancy. In a new study, researchers report they have added new capabilities to an experimental drug agent that previously ...
Biochemistry
Nov 9, 2015
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32
In his mind, Basil Hubbard can already picture a new world of therapeutic treatments for millions of patients just over the horizon. It's a future in which diseases like muscular dystrophy, cystic fibrosis and many others ...
Biotechnology
Aug 10, 2015
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In a new study that could ultimately lead to many new medicines, scientists from the Florida campus of The Scripps Research Institute (TSRI) have adapted a chemical approach to turn diseased cells into unique manufacturing ...
Biochemistry
Sep 2, 2014
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Children with Duchenne muscular dystrophy often die as young adults from heart and breathing complications. However, scientists have been puzzled for decades by the fact that laboratory mice bearing the same genetic mutation ...
Cell & Microbiology
Jul 7, 2013
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Many scientists use animals to model human diseases. Mice can be obese or display symptoms of Parkinson's disease. Rats get Alzheimer's and diabetes.
Cell & Microbiology
Jun 27, 2013
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