News tagged with enzyme replacement therapy
New test spots early signs of mucopolysaccharidoses -- inherited metabolic disorders
A team of scientists, led by researchers at the University of California, San Diego School of Medicine and Zacharon Pharmaceuticals, have developed a simple, reliable test for identifying biomarkers for mucopolysaccharidoses ...
Jan 08, 2012 |
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Research supports newborn screening and early treatment for rare genetic disorder, MPS I
In a study that supports the need for newborn screening and early treatment for a rare genetic disorder, researchers at Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center (LA BioMed) and ...
Medicine & Health / Medical research
Dec 01, 2010 |
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Inventive approach may improve enzyme replacement therapy for Fabry disease
A new study uses a creative structure-based remodeling strategy to design a therapeutic protein that exhibits significant advantages over currently available treatments for a rare disease that often leads to cardiac and renal ...
Oct 22, 2009 |
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Transplanted human stem cells prolong survival in mouse model of rare brain disease
A new study finds substantial improvement in a mouse model of a rare, hereditary neurodegenerative disease after transplantation of normal human neural stem cells. The research findings, published by Cell Press in the September ...
Medicine & Health / Medical research
Sep 03, 2009 |
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Enzyme therapy slows kidney function decline
For men with Fabry disease, enzyme replacement therapy (ERT) with agalsidase alfa slows deterioration of kidney function, reports a study in the online edition of the Journal of the American Society of Nephrology (JASN). "The results ...
Medicine & Health / Diseases, Conditions, Syndromes
Apr 08, 2009 |
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