News tagged with adrenoleukodystrophy
Gene therapy technique slows ALD brain disease
A strategy that combines gene therapy with blood stem cell therapy may be a useful tool for treating a fatal brain disease, French researchers have found. These findings appear in the 6 November 2009 issue ...
Medicine & Health / Medical research
Nov 05, 2009 |
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Search results for adrenoleukodystrophy
Gene therapy success in Wiskott-Aldrich syndrome
A pediatric immunologist at The Children's Hospital of Philadelphia collaborated with European gene therapy researchers who achieved marked clinical improvements in two young children with Wiskott-Aldrich syndrome, a very ...
Medicine & Health / Medical research
Nov 15, 2010 |
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Engineered version of HIV is used to cure genetic blood disorder
For the second time, researchers have used the HIV virus in gene therapy to cure a severe genetic disease, this time the blood disorder beta-thalassemia, which causes life-threatening anemia.
Medicine & Health / Medical research
Sep 16, 2010 |
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Nature publishes results of gene therapy treatment in phase 1/2 beta-thalassemia study
bluebird bio (formerly Genetix Pharmaceuticals Inc.) today announced publication in the journal Nature of its promising Phase 1/2 data highlighting positive results of LentiGlobin gene therapy treatment in a young adult ...
Sep 15, 2010 |
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Researchers find mechanism that could prevent or treat deadly peroxisome diseases
University of Alberta medical researchers have made a major breakthrough in understanding a group of deadly disorders that includes the disease made famous in the movie Lorenzo's Oil.
Medicine & Health / Medical research
Jan 07, 2010 |
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Rare disease claims children early
Soon after her second son was born in September 2006, Carolina Alfaro noticed he had trouble nursing. In the following months, Diego was unable to roll over or lift his head when he was laid on a blanket.
Medicine & Health / Diseases, Conditions, Syndromes
May 29, 2009 |
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Human stem cells show promise against fatal children's diseases
Scientists have used human stem cells to dramatically improve the condition of mice with a neurological condition similar to a set of diseases in children that are invariably fatal, according to an article in the June issue ...
Medicine & Health / Medical research
Jun 04, 2008 |
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List of search results for adrenoleukodystrophy
